Lentiviral Gene Therapy Approach for Haemoglobinopathies
Lentiviral Gene Therapy Approach for Haemoglobinopathies Novel beta and gamma globin gene addition vectors have…
AAV Antibody Assay
AAV Antibody Assay Established capsid and peptide ELISA as well as Transduction Inhibition Assays (TIAs)…
iPSC Technology
IPSC Technology An efficient method for the generation of iPSCs from erythroid progenitors has been…
Gene Editing Approach for Haemoglobinopathies
Gene Editing Approach for Haemoglobinopathies Novel targets have been identified in the BCL11A enhancer for…